Webcast: ADA-SCID and your clinical practice
For optimal display of the webcast, enable flash player through your browser settings
Panel
- Moderator: Dr Andrew Gennery
Newcastle University and Great North Children’s Hospital, Newcastle upon Tyne, UK - Dr Claire Booth
UCL Great Ormond Street Institute of Child Health, London, UK - Dr Maria Pia Cicalese
San Raffaele Scientific Institute, Milan, Italy
Summary
Improve your knowledge of the diagnosis and management of ADA-SCID in every day clinical practice. In the context of patient cases, our expert panel discuss topics including the screening and detection of ADA-SCID, the current care pathway and the increasing role novel gene therapies look to play in the treatment of patients with this rare immune disorder.
Learning objectives
At the end of the webcast, participants will be able to:
- Explain the underlying biology as well as the screening and detection methods for ADA-SCID.
- Describe and debate the current treatment algorithm for ADA deficiency.
- Summarise the latest advances in gene therapy for ADA-SCID, notably gammaretroviral and lentiviral vector gene therapies, and how these novel treatments can be applied to every day clinical practice.
Evaluation
Your opinion matters to us. Please complete our short survey after watching the video.